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Disease Reportsduchenne muscular dystrophy
MeSH D020388 - duchenne muscular dystrophy
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Competitive Landscape
Events Timeline
Commercial
Clinical Trials
Competitive landscape
D009136:Muscular dystrophies
0 Companies
0 Drugs
Success rate
D040181:X-linked genetic diseases
0 Companies
0 Drugs
Success rate
D020388: 
Duchenne muscular dystrophy
$
Success rate
Events Timeline
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Commercial
Company Name
Drug Name
Trade Name
Patent Expires
Approval Date
Revenue
Period
Catalyst PharmaceuticalsVAMOROLONE Agamree 2029-05-28 2023-10-26 $1.174 M Y2024 
Nippon ShinyakuViltolarsen Viltepso 2031-08-31 2020-08-12   
PTC TherapeuticsDeflazacort Emflaza  2017-02-09 $258 M Q2/23-Q1/24 
Ataluren Translarna  2014-07-31 $344.3 M Q2/23-Q1/24 
Sarepta TherapeuticsCasimersen Amondys 2025-06-28 2021-02-25 $33.784 M Y2021 
Eteplirsen Exondys 2025-06-28 2016-09-19 $447.046 M Q3/20-Q3/21 
Golodirsen Vyondys 2025-06-28 2019-12-12 $74.275 M Q3/20-Q3/21 
Clinical Trials
Historical Success Rate
Phase 1
59%
19/32
Phase 2
63%
15/24
Phase 3
45%
13/29
Approved: 7Overall Success rate: 17%
All Clinical Trials
Therapeutic Areas:
All
Classification:
All
Approval:
All
Status:
All
Phases:
All
Company name
Phase 1
Phase 2
Phase 3
Phase 4
Drug Name
Italfarmaco
Nippon Shinyaku
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